中国科学院机构知识库网格
Chinese Academy of Sciences Institutional Repositories Grid
MM201-Mediated Gene Activation Therapy Enhances Utrophin Expression and Improves Muscle Function in Duchenne Muscular Dystrophy

文献类型:期刊论文

作者Li, Guoling5; Lin, Jiajia4; Li, Tong3; Zhang, Hainan3; Yuan, Yiqun5; Zhang, Xin2,5; Shi, Linyu5; Luk, Alvin1; Yang, Hui3,5
刊名MOLECULAR THERAPY
出版日期2025-04-28
卷号33期号:4页码:3
ISSN号1525-0016
WOS研究方向Biotechnology & Applied Microbiology ; Genetics & Heredity ; Research & Experimental Medicine
语种英语
WOS记录号WOS:001573749200200
出版者CELL PRESS
源URL[http://119.78.100.183/handle/2S10ELR8/319792]  
专题中国科学院上海药物研究所
作者单位1.Huidagene Therapeut Inc, Clinton, NJ USA
2.HuidaGene Therapeut, Clinton, NJ USA
3.Chinese Acad Sci, Shanghai Inst Mat Med, Shanghai, Peoples R China
4.Fujian Med Univ, Affiliated Hosp 1, Dept Neurol, Fuzhou, Peoples R China
5.HuidaGene Therapeut Co Ltd, Shanghai, Peoples R China
推荐引用方式
GB/T 7714
Li, Guoling,Lin, Jiajia,Li, Tong,et al. MM201-Mediated Gene Activation Therapy Enhances Utrophin Expression and Improves Muscle Function in Duchenne Muscular Dystrophy[J]. MOLECULAR THERAPY,2025,33(4):3.
APA Li, Guoling.,Lin, Jiajia.,Li, Tong.,Zhang, Hainan.,Yuan, Yiqun.,...&Yang, Hui.(2025).MM201-Mediated Gene Activation Therapy Enhances Utrophin Expression and Improves Muscle Function in Duchenne Muscular Dystrophy.MOLECULAR THERAPY,33(4),3.
MLA Li, Guoling,et al."MM201-Mediated Gene Activation Therapy Enhances Utrophin Expression and Improves Muscle Function in Duchenne Muscular Dystrophy".MOLECULAR THERAPY 33.4(2025):3.

入库方式: OAI收割

来源:上海药物研究所

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