MM201-Mediated Gene Activation Therapy Enhances Utrophin Expression and Improves Muscle Function in Duchenne Muscular Dystrophy
文献类型:期刊论文
| 作者 | Li, Guoling5; Lin, Jiajia4; Li, Tong3; Zhang, Hainan3; Yuan, Yiqun5; Zhang, Xin2,5; Shi, Linyu5; Luk, Alvin1; Yang, Hui3,5 |
| 刊名 | MOLECULAR THERAPY
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| 出版日期 | 2025-04-28 |
| 卷号 | 33期号:4页码:3 |
| ISSN号 | 1525-0016 |
| WOS研究方向 | Biotechnology & Applied Microbiology ; Genetics & Heredity ; Research & Experimental Medicine |
| 语种 | 英语 |
| WOS记录号 | WOS:001573749200200 |
| 出版者 | CELL PRESS |
| 源URL | [http://119.78.100.183/handle/2S10ELR8/319792] ![]() |
| 专题 | 中国科学院上海药物研究所 |
| 作者单位 | 1.Huidagene Therapeut Inc, Clinton, NJ USA 2.HuidaGene Therapeut, Clinton, NJ USA 3.Chinese Acad Sci, Shanghai Inst Mat Med, Shanghai, Peoples R China 4.Fujian Med Univ, Affiliated Hosp 1, Dept Neurol, Fuzhou, Peoples R China 5.HuidaGene Therapeut Co Ltd, Shanghai, Peoples R China |
| 推荐引用方式 GB/T 7714 | Li, Guoling,Lin, Jiajia,Li, Tong,et al. MM201-Mediated Gene Activation Therapy Enhances Utrophin Expression and Improves Muscle Function in Duchenne Muscular Dystrophy[J]. MOLECULAR THERAPY,2025,33(4):3. |
| APA | Li, Guoling.,Lin, Jiajia.,Li, Tong.,Zhang, Hainan.,Yuan, Yiqun.,...&Yang, Hui.(2025).MM201-Mediated Gene Activation Therapy Enhances Utrophin Expression and Improves Muscle Function in Duchenne Muscular Dystrophy.MOLECULAR THERAPY,33(4),3. |
| MLA | Li, Guoling,et al."MM201-Mediated Gene Activation Therapy Enhances Utrophin Expression and Improves Muscle Function in Duchenne Muscular Dystrophy".MOLECULAR THERAPY 33.4(2025):3. |
入库方式: OAI收割
来源:上海药物研究所
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