CRISPR-hfCas12Max-Mediated Therapy HG303 Improves Neuromuscular Function and Survival in Amyotrophic Lateral Sclerosis Models
文献类型:期刊论文
| 作者 | Yang, Dong9; Guo, Aiguo9; Li, Tong8; Cradick, T. J.4,5,6,7; Luk, Alvin3; Yang, Hui1,2; Shi, Linyu9 |
| 刊名 | MOLECULAR THERAPY
![]() |
| 出版日期 | 2025-04-28 |
| 卷号 | 33期号:4页码:4 |
| ISSN号 | 1525-0016 |
| WOS研究方向 | Biotechnology & Applied Microbiology ; Genetics & Heredity ; Research & Experimental Medicine |
| 语种 | 英语 |
| WOS记录号 | WOS:001493880500075 |
| 出版者 | CELL PRESS |
| 源URL | [http://119.78.100.183/handle/2S10ELR8/321126] ![]() |
| 专题 | 中国科学院上海药物研究所 |
| 作者单位 | 1.Chinese Acad Sci, Shanghai Inst Meteria Med, Shanghai, Peoples R China 2.HuidaGene Therapeut Co Ltd, Shanghai, Peoples R China 3.Huidagene Therapeut Inc, Clinton, NJ USA 4.Cholgene Therapeut, Middletown, MA USA 5.Cholgene Therapeut, Clinton, NJ USA 6.Cholgene Therapeut, Middletown, DE USA 7.HuidaGene Therapeut, Clinton, NJ USA 8.Chinese Acad Sci, Shanghai Inst Mat Med, Shanghai, Peoples R China 9.HuidaGene Therapeut Co Ltd, Shanghai, Peoples R China |
| 推荐引用方式 GB/T 7714 | Yang, Dong,Guo, Aiguo,Li, Tong,et al. CRISPR-hfCas12Max-Mediated Therapy HG303 Improves Neuromuscular Function and Survival in Amyotrophic Lateral Sclerosis Models[J]. MOLECULAR THERAPY,2025,33(4):4. |
| APA | Yang, Dong.,Guo, Aiguo.,Li, Tong.,Cradick, T. J..,Luk, Alvin.,...&Shi, Linyu.(2025).CRISPR-hfCas12Max-Mediated Therapy HG303 Improves Neuromuscular Function and Survival in Amyotrophic Lateral Sclerosis Models.MOLECULAR THERAPY,33(4),4. |
| MLA | Yang, Dong,et al."CRISPR-hfCas12Max-Mediated Therapy HG303 Improves Neuromuscular Function and Survival in Amyotrophic Lateral Sclerosis Models".MOLECULAR THERAPY 33.4(2025):4. |
入库方式: OAI收割
来源:上海药物研究所
浏览0
下载0
收藏0
其他版本
除非特别说明,本系统中所有内容都受版权保护,并保留所有权利。

