中国科学院机构知识库网格
Chinese Academy of Sciences Institutional Repositories Grid
CRISPR-hfCas12Max-Mediated Therapy HG303 Improves Neuromuscular Function and Survival in Amyotrophic Lateral Sclerosis Models

文献类型:期刊论文

作者Yang, Dong9; Guo, Aiguo9; Li, Tong8; Cradick, T. J.4,5,6,7; Luk, Alvin3; Yang, Hui1,2; Shi, Linyu9
刊名MOLECULAR THERAPY
出版日期2025-04-28
卷号33期号:4页码:4
ISSN号1525-0016
WOS研究方向Biotechnology & Applied Microbiology ; Genetics & Heredity ; Research & Experimental Medicine
语种英语
WOS记录号WOS:001493880500075
出版者CELL PRESS
源URL[http://119.78.100.183/handle/2S10ELR8/321126]  
专题中国科学院上海药物研究所
作者单位1.Chinese Acad Sci, Shanghai Inst Meteria Med, Shanghai, Peoples R China
2.HuidaGene Therapeut Co Ltd, Shanghai, Peoples R China
3.Huidagene Therapeut Inc, Clinton, NJ USA
4.Cholgene Therapeut, Middletown, MA USA
5.Cholgene Therapeut, Clinton, NJ USA
6.Cholgene Therapeut, Middletown, DE USA
7.HuidaGene Therapeut, Clinton, NJ USA
8.Chinese Acad Sci, Shanghai Inst Mat Med, Shanghai, Peoples R China
9.HuidaGene Therapeut Co Ltd, Shanghai, Peoples R China
推荐引用方式
GB/T 7714
Yang, Dong,Guo, Aiguo,Li, Tong,et al. CRISPR-hfCas12Max-Mediated Therapy HG303 Improves Neuromuscular Function and Survival in Amyotrophic Lateral Sclerosis Models[J]. MOLECULAR THERAPY,2025,33(4):4.
APA Yang, Dong.,Guo, Aiguo.,Li, Tong.,Cradick, T. J..,Luk, Alvin.,...&Shi, Linyu.(2025).CRISPR-hfCas12Max-Mediated Therapy HG303 Improves Neuromuscular Function and Survival in Amyotrophic Lateral Sclerosis Models.MOLECULAR THERAPY,33(4),4.
MLA Yang, Dong,et al."CRISPR-hfCas12Max-Mediated Therapy HG303 Improves Neuromuscular Function and Survival in Amyotrophic Lateral Sclerosis Models".MOLECULAR THERAPY 33.4(2025):4.

入库方式: OAI收割

来源:上海药物研究所

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