CRISPR-Cas13 Gene Editing Therapy Targeting VEGFA Demonstrated Early Efficacy in Neovascular Age-Related Macular Degeneration
文献类型:期刊论文
| 作者 | Xing, Dongjun5,6; Liu, Boshi5,6; Liu, Weiwei4; Zhang, Shuaishuai4; Jiang, Yuhan4; Shi, Linyu4; Yang, Hui3,4; Zhang, Xin2,4; Luk, Alvin1; Yuan, Yiqun4 |
| 刊名 | MOLECULAR THERAPY
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| 出版日期 | 2025-04-28 |
| 卷号 | 33期号:4页码:2 |
| ISSN号 | 1525-0016 |
| WOS研究方向 | Biotechnology & Applied Microbiology ; Genetics & Heredity ; Research & Experimental Medicine |
| 语种 | 英语 |
| WOS记录号 | WOS:001493880500034 |
| 出版者 | CELL PRESS |
| 源URL | [http://119.78.100.183/handle/2S10ELR8/321132] ![]() |
| 专题 | 中国科学院上海药物研究所 |
| 作者单位 | 1.Huidagene Therapeut Inc, Clinton, NJ USA 2.HuidaGene Therapeut, Clinton, NJ USA 3.Chinese Acad Sci, Shanghai Inst Meteria Med, Shanghai, Peoples R China 4.HuidaGene Therapeut Co Ltd, Shanghai, Peoples R China 5.Tianjin Med Univ, Hosp Eye, Inst Eye, Tianjin 300384, Peoples R China 6.Tianjin Med Univ, Hosp Eye, Natl Res Ctr Ocular Dis, Tianjin Branch,Sch Optometry, Tianjin 300384, Peoples R China |
| 推荐引用方式 GB/T 7714 | Xing, Dongjun,Liu, Boshi,Liu, Weiwei,et al. CRISPR-Cas13 Gene Editing Therapy Targeting VEGFA Demonstrated Early Efficacy in Neovascular Age-Related Macular Degeneration[J]. MOLECULAR THERAPY,2025,33(4):2. |
| APA | Xing, Dongjun.,Liu, Boshi.,Liu, Weiwei.,Zhang, Shuaishuai.,Jiang, Yuhan.,...&Li, Xiaorong.(2025).CRISPR-Cas13 Gene Editing Therapy Targeting VEGFA Demonstrated Early Efficacy in Neovascular Age-Related Macular Degeneration.MOLECULAR THERAPY,33(4),2. |
| MLA | Xing, Dongjun,et al."CRISPR-Cas13 Gene Editing Therapy Targeting VEGFA Demonstrated Early Efficacy in Neovascular Age-Related Macular Degeneration".MOLECULAR THERAPY 33.4(2025):2. |
入库方式: OAI收割
来源:上海药物研究所
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