中国科学院机构知识库网格
Chinese Academy of Sciences Institutional Repositories Grid
HG204 CRISPR-Cas13 RNA-Editing Therapy for MECP2 Duplication Syndrome: Preclinical Success to First-in-Human Study

文献类型:期刊论文

作者Yang, Dong4; Yuan, Yiqun4; Zhang, Xin4; Luk, Alvin3; Yang, Hui1,2; Shi, Linyu4
刊名MOLECULAR THERAPY
出版日期2025-04-28
卷号33期号:4页码:3
ISSN号1525-0016
WOS研究方向Biotechnology & Applied Microbiology ; Genetics & Heredity ; Research & Experimental Medicine
语种英语
WOS记录号WOS:001521594200223
出版者CELL PRESS
源URL[http://119.78.100.183/handle/2S10ELR8/321162]  
专题中国科学院上海药物研究所
作者单位1.Chinese Acad Sci, Shanghai Inst Meteria Med, Shanghai, Peoples R China
2.HuidaGene Therapeut Co Ltd, Shanghai, Peoples R China
3.Huidagene Therapeut Inc, Clinton, NJ USA
4.HuidaGene Therapeut Co Ltd, Shanghai, Peoples R China
推荐引用方式
GB/T 7714
Yang, Dong,Yuan, Yiqun,Zhang, Xin,et al. HG204 CRISPR-Cas13 RNA-Editing Therapy for MECP2 Duplication Syndrome: Preclinical Success to First-in-Human Study[J]. MOLECULAR THERAPY,2025,33(4):3.
APA Yang, Dong,Yuan, Yiqun,Zhang, Xin,Luk, Alvin,Yang, Hui,&Shi, Linyu.(2025).HG204 CRISPR-Cas13 RNA-Editing Therapy for MECP2 Duplication Syndrome: Preclinical Success to First-in-Human Study.MOLECULAR THERAPY,33(4),3.
MLA Yang, Dong,et al."HG204 CRISPR-Cas13 RNA-Editing Therapy for MECP2 Duplication Syndrome: Preclinical Success to First-in-Human Study".MOLECULAR THERAPY 33.4(2025):3.

入库方式: OAI收割

来源:上海药物研究所

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