中国科学院机构知识库网格
Chinese Academy of Sciences Institutional Repositories Grid
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CRISPR-hfCas12Max Genome Editing Therapy Demonstrates Preclinical Efficacy and Early Clinical Benefit in Duchenne Muscular Dystrophy 期刊论文  OAI收割
MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 3
作者:  
Luk, Alvin;  Lin, Jiajia;  Jin, Ming;  Li, Zhifang;  Li, Tong
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CRISPR-hfCas12Max-Mediated Therapy HG303 Improves Neuromuscular Function and Survival in Amyotrophic Lateral Sclerosis Models 期刊论文  OAI收割
MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 4
作者:  
Yang, Dong;  Guo, Aiguo;  Li, Tong;  Cradick, T. J.;  Luk, Alvin
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AI-Assisted Development of Compact Base Editors for Enhanced Efficiency and Specificity with Broad Targeting Range 期刊论文  OAI收割
MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 2
作者:  
Kong, Xiangfeng;  Xue, Yanbing;  Li, Guoling;  Li, Jinhui;  Chen, Yihong
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hfCas12Max: Engineered CRISPR Nuclease for Safer and Effective CGT 期刊论文  OAI收割
MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 2
作者:  
Molnar, Michael;  Zhang, Hainan;  Yang, Hui;  Holden, Kevin;  Luk, Alvin
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