中国科学院机构知识库网格
Chinese Academy of Sciences Institutional Repositories Grid
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浏览/检索结果: 共59条,第1-10条 帮助

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A Comprehensive Study of AAV Tropism in the Marmoset Brain 期刊论文  OAI收割
NEUROSCIENCE BULLETIN, 2026, 页码: 10
作者:  
Fang, Kailun;  Liu, Hailin;  Yao, Yuting;  Xu, Zhen;  Liu, Xinyu
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CRISPR-hfCas12Max Genome Editing Therapy Demonstrates Preclinical Efficacy and Early Clinical Benefit in Duchenne Muscular Dystrophy 期刊论文  OAI收割
MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 3
作者:  
Luk, Alvin;  Lin, Jiajia;  Jin, Ming;  Li, Zhifang;  Li, Tong
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CRISPR-hfCas12Max-Mediated Therapy HG303 Improves Neuromuscular Function and Survival in Amyotrophic Lateral Sclerosis Models 期刊论文  OAI收割
MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 4
作者:  
Yang, Dong;  Guo, Aiguo;  Li, Tong;  Cradick, T. J.;  Luk, Alvin
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CRISPR-Cas13 Gene Editing Therapy Targeting VEGFA Demonstrated Early Efficacy in Neovascular Age-Related Macular Degeneration 期刊论文  OAI收割
MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 2
作者:  
Xing, Dongjun;  Liu, Boshi;  Liu, Weiwei;  Zhang, Shuaishuai;  Jiang, Yuhan
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AI-Assisted Development of Compact Base Editors for Enhanced Efficiency and Specificity with Broad Targeting Range 期刊论文  OAI收割
MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 2
作者:  
Kong, Xiangfeng;  Xue, Yanbing;  Li, Guoling;  Li, Jinhui;  Chen, Yihong
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CRISPR-hfCas13Y RNA-targeting Therapy Restores Cognitive Function by Reducing BACE1 or MAPT in Alzheimer's Disease Model 期刊论文  OAI收割
MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 3
作者:  
Yao, Yinan;  Ma, Hanbo;  Liu, Yuanhua;  Li, Tong;  Zhang, Xin
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MM201-Mediated Gene Activation Therapy Enhances Utrophin Expression and Improves Muscle Function in Duchenne Muscular Dystrophy 期刊论文  OAI收割
MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 3
作者:  
Li, Guoling;  Lin, Jiajia;  Li, Tong;  Zhang, Hainan;  Yuan, Yiqun
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Distribution of scoliosis in 2.22 million adolescents in mainland China: A population-wide analysis 期刊论文  OAI收割
JOURNAL OF GLOBAL HEALTH, 2024, 卷号: 14, 页码: 4117
作者:  
Xu, Shuai;  Li, Kexin;  Jin, Linyu;  Dong, Yanhui;  Liang, Yan
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中国散裂中子源伴生质子辐照实验平台及其技术参数的确定 期刊论文  OAI收割
现代应用物理, 2024, 卷号: 15, 期号: 02, 页码: 96-104
作者:  
谭志新;  敬罕涛;  樊瑞睿;  黄良生;  蒋伟
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高速列车内飞沫传播特性及抑制方法研究 期刊论文  OAI收割
暖通空调, 2023, 卷号: 53, 期号: S2, 页码: 232-236
作者:  
刘雯;  李徽;  李林蔚;  鞠胜军
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