机构

• 上海药物研究所 [9]

采集方式

• OAI收割 [9]

内容类型

• 期刊论文 [9]

发表日期

• 2025 [9]

学科主题

筛选

浏览/检索结果: 共9条，第1-9条 帮助 条数/页： 5101520253035404550556065707580859095100 排序方式： 请选择提交时间升序提交时间降序发表日期升序发表日期降序题名升序题名降序作者升序作者降序 CRISPR-hfCas12Max Genome Editing Therapy Demonstrates Preclinical Efficacy and Early Clinical Benefit in Duchenne Muscular Dystrophy 期刊论文  OAI收割 MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 3 作者:  Luk, Alvin;  Lin, Jiajia;  Jin, Ming;  Li, Zhifang;  Li, Tong   |  收藏  |   CRISPR-hfCas12Max-Mediated Therapy HG303 Improves Neuromuscular Function and Survival in Amyotrophic Lateral Sclerosis Models 期刊论文  OAI收割 MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 4 作者:  Yang, Dong;  Guo, Aiguo;  Li, Tong;  Cradick, T. J.;  Luk, Alvin   |  收藏  |   CRISPR-Cas13 Gene Editing Therapy Targeting VEGFA Demonstrated Early Efficacy in Neovascular Age-Related Macular Degeneration 期刊论文  OAI收割 MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 2 作者:  Xing, Dongjun;  Liu, Boshi;  Liu, Weiwei;  Zhang, Shuaishuai;  Jiang, Yuhan   |  收藏  |   AI-Assisted Development of Compact Base Editors for Enhanced Efficiency and Specificity with Broad Targeting Range 期刊论文  OAI收割 MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 2 作者:  Kong, Xiangfeng;  Xue, Yanbing;  Li, Guoling;  Li, Jinhui;  Chen, Yihong   |  收藏  |   HG204 CRISPR-Cas13 RNA-Editing Therapy for MECP2 Duplication Syndrome: Preclinical Success to First-in-Human Study 期刊论文  OAI收割 MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 3 作者:  Yang, Dong;  Yuan, Yiqun;  Zhang, Xin;  Luk, Alvin;  Yang, Hui   |  收藏  |   CRISPR-hfCas13Y RNA-targeting Therapy Restores Cognitive Function by Reducing BACE1 or MAPT in Alzheimer's Disease Model 期刊论文  OAI收割 MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 3 作者:  Yao, Yinan;  Ma, Hanbo;  Liu, Yuanhua;  Li, Tong;  Zhang, Xin   |  收藏  |   hfCas12Max: Engineered CRISPR Nuclease for Safer and Effective CGT 期刊论文  OAI收割 MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 2 作者:  Molnar, Michael;  Zhang, Hainan;  Yang, Hui;  Holden, Kevin;  Luk, Alvin   |  收藏  |   CRISPR-hfCas12Max-Mediated DNA Editing Restores Motor Function in Spinocerebellar Ataxia Type 3 期刊论文  OAI收割 MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 2 作者:  Yang, Dong;  Huang, Zhuoying;  Luk, Alvin;  Shi, Linyu;  Yang, Hui   |  收藏  |   MM201-Mediated Gene Activation Therapy Enhances Utrophin Expression and Improves Muscle Function in Duchenne Muscular Dystrophy 期刊论文  OAI收割 MOLECULAR THERAPY, 2025, 卷号: 33, 期号: 4, 页码: 3 作者:  Li, Guoling;  Lin, Jiajia;  Li, Tong;  Zhang, Hainan;  Yuan, Yiqun   |  收藏  |